Generale
Lupin Neurosciences si impegna a collaborare con gli operatori sanitari per sviluppare soluzioni basate sulla scienza che vadano al di là dell’accesso a opzioni terapeutiche che cambiano la vita ed ottimizzan la cura di pazienti affetti da malattie neurologiche sottoservite.
30th Annual international Congress of the World Muscle Society, Austria, Vienna, 7-11 October 2025
Myotonic dystrophy
369P
TRACK DM: design of longitudinal natural history study in people with myotonic dystrophy linking retrospective data with prospective follow-up
Guillaume Bassez, Melinda Gyenge, Alla Zozulya Weidenfeller
Poster: Poster
377P
CoreDMScope_ENSA (RevEal the burdeN in daily life in myotonic dyStrophy due to myotoniA): study design compares patient-reported and clinical outcomes
Melinda Gyenge, Guillaume Bassez, Razak Ellafi, Alla Zozulya Weidenfeller, Regis Dufresne
Poster: Poster
Non-dystrophic myotonia
67P
Mexiletine Paediatric Investigation Plan, PIP4 study: safety, pharmacokinetic and efficacy findings in children with myotonia
Christine Barnérias, Arnaud Isapof, Jean-Yves Hogrel, Helen Pentikis, Nikki Adetoro, Alla Zozulya Weidenfeller
Poster: Poster